The global Duchenne muscular dystrophy drugs market size reached USD'2.04 bn in 2022.
Looking forward, the publisher expects the market to reach USD 4bn by 2028, exhibiting a CAGR of 11.88% during 2022-2028.
Companies Mentioned
FibroGen Inc.
Italfarmaco S.p.A.
NS Pharma Inc. (Nippon Shinyaku Co. Ltd.)
PTC Therapeutics Inc.
Santhera Pharmaceuticals
Sarepta Therapeutics Inc
The rising prevalence of Duchenne muscular dystrophy among the masses, the increasing number of new product approvals and launches, and favorable government initiatives providing good reimbursement policies, along with promoting target-specific treatments, represent some of the key factors driving the market.
Duchenne muscular dystrophy drugs are utilized to treat a severe X-linked genetic disorder of a progressive form of muscular dystrophy that primarily affects the male population, and rarely females as well.
The symptoms of this disorder include difficulty walking, standing, and sitting, as well as speech difficulties, which can result in progressive weakness and loss, also known as atrophy, in the skeletal and heart muscles.
The DMD drugs enhance cardiac and pulmonary functions in patients by targeting cardiac and skeletal muscles. Dystrophin is a key protein that maintains muscular integrity, and its absence or abnormality causes DMD.
As a result, most of the drugs for the treatment of DMD are dystrophin-based.
Some of the other primary treatment strategies for DMD also include genetic therapies linked to specific mutations which restore dystrophin production, membrane stabilization or upregulation of compensatory proteins, and a reduction of the inflammatory cascade and/or enhancement of muscle regeneration.
The rising number of new product approvals and launches by the major manufacturers is a significant factor driving the growth of the market.
This can be attributed to the growing incidences of Duchenne muscular dystrophy among the masses.
In line with this, a considerable rise in clinical trials, along with the presence of strong pipeline of products, is providing an impetus to the market.
Moreover, the advent of mutation-specific therapies due to continual innovations in diagnostics is also impacting the market positively.
Besides this, extensive research and development activities focusing on accurate diagnosis and treatment of DMD for under served categories, such as infants, females, and non-ambulant patients, are propelling the market.
However, the shortage of standardized procedures for the examination of the clinical efficacy of drugs, delayed diagnosis and prediction, and the rising costs of genetic therapeutics are acting as growth-restraining factors for the market.
On the contrary, favorable government initiatives providing good reimbursement policies, along with promoting target-specific treatments, are contributing to the market growth.
Some of the other factors creating lucrative growth opportunities in the market include rapid urbanization, improving medical infrastructure, emerging trend of product premiumization, and inflating disposable incomes of the masses.
Key Market Segmentation:
The publisher provides an analysis of the key trends in each segment of the global Duchenne muscular dystrophy drugs market, along with forecasts at the global, regional, and country level from 2023-2028.
Our report has categorized the market based on product type, therapeutic approach, and end user.
Product Type Insights:
Corticosteroids
Prednisolone
Prednisone
Deflazacort
Pain Management Drugs
The report has provided a detailed breakup and analysis of the Duchenne muscular dystrophy drugs market based on the product type.
This includes corticosteroids (prednisolone, prednisone and deflazacort) and pain management drugs. According to the report, corticosteroids represented the largest segment.
Therapeutic Approach Insights:
Mutation Suppression
Exon Skipping
Steroid Therapy
The report has provided a detailed breakup and analysis of the Duchenne muscular dystrophy drugs market based on the therapeutic approach.
This includes mutation suppression, exon skipping, and steroid therapy. According to the report, exon skipping represented the largest segment.
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