Therapy Areas: Hereditary Disorders
7 September 2023 - SpliSense, an Israel-based biopharmaceutical company, announced on Wednesday that it has completed a first-in-human, Phase one clinical trial of SPL84, the company's lead inhal...
1 September 2023 - Alcresta Therapeutics, Inc., a US-based commercial-stage company involved in developing and commercialising novel enzyme-based products, announced on Thursday that the US FDA has ap...
10 August 2023 - - US-based Vertex Pharmaceuticals Inc. (NASDAQ: VRTX) has announced publication in the New England Journal of Medicine (NEJM) of preclinical data and the results from i...
13 July 2023 - Medical technology company Inogen Inc (Nasdaq:INGN) announcedon Thursday that it has entered a definitive agreement to purchase Physio-Assist SAS, a French company.Physio-Assist's ...
5 July 2023 - Biotechnology company Vertex Pharmaceuticals (NASDAQ:VRTX) announced on Wednesday that it has obtained approval from the European Commission to extend the label of ORKAMBI (lumacaftor/iv...
27 June 2023 - cystetic Medicines, Inc., a US-based clinical-stage biotechnology company, announced on Monday it has dosed its first healthy volunteer with CM001 in a Phase one clinical trial.CM001 is...
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