Therapy Areas: Hereditary Disorders
22 August 2019 - The US Food and Drug Administration (FDA) has accepted a new drug application (NDA) for United States-based Vertex Pharmaceuticals' VX-445 (elexacaftor), tezacaftor and ivacaftor...
26 July 2019 - - US-based biotechnology company Vertex Pharmaceuticals Inc.'s (NASDAQ: VRTX) board of directors has approved the planned transition of chairman, president and chief executive offi...
23 July 2019 - - The Cystic Fibrosis Foundation has announced the recipients of its fourth annual Impact Grants, which provide funding to people with cystic fibrosis who are leading unique projects in...
22 July 2019 - United States-based Aridis Pharmaceuticals Inc (Nasdaq: ARDS) has received Orphan Drug Designation from the European Medicines Agency (EMA) for its AR-501, the company's inhaled fo...
9 July 2019 - - Switzerland-based Octapharma presented new data on the benefits of Nuwiq in patients with haemophilia A during a scientific symposium at the 27th International Society on Thrombos...
27 June 2019 - Biopharmaceutical company Aridis Pharmaceuticals Inc (Nasdaq:ARDS) reported on Wednesday that it has received the US Food and Drug Administration's (FDA) orphan drug designation (O...
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