Therapy Areas: Hereditary Disorders
9 July 2019 - - Switzerland-based Octapharma presented new data on the benefits of Nuwiq in patients with haemophilia A during a scientific symposium at the 27th International Society on Thrombos...
27 June 2019 - Biopharmaceutical company Aridis Pharmaceuticals Inc (Nasdaq:ARDS) reported on Wednesday that it has received the US Food and Drug Administration's (FDA) orphan drug designation (O...
24 June 2019 - Public health agency the US Food and Drug Administration announced Friday that it has expanded the indication of Symdeko tablets for the treatment of paediatric patients ages six years ...
20 June 2019 - - US-based commercial-stage company Alcresta Therapeutics Inc has appointed Daniel Orlando as its chief executive officer and member of the board of directors, the company said.
O...
17 June 2019 - - US-based orphan lung disease company Savara Inc. (NASDAQ: SVRA) has received disappointing top line data from IMPALA, a pivotal Phase 3 clinical study evaluating Molgradex, an in...
3 June 2019 - United States-based Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) has chosen the triple combination of the new corrector VX-445 (elexacaftor), tezacaftor and ivacaftor to submit for...
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